Life Sciences

Cumulative motor index in spinal muscular atrophy after gene therapy: baseline predicts maximal recovery

Published on - Clinical Neurophysiology

Authors: Rémi Barrois, Christine Barnerias, Anaïs Hervé, Elodie Deladrière, Brigitte Fauroux, Lucie Griffon, Sonia Khirani, Clément Poirault, Isabelle Desguerre, Cyril Gitiaux